In June, the monoclonal antibody garadacimab (Andembry) was approved for prevention of HAE attacks at a dose of once monthly ...

Sarepta is facing a number of issues currently, including platform-level safety concerns, management credibility issues, etc.

The approval makes donidalorsen the only treatment in the US for hereditary angioedema that is an RNA-targeted prophylactic.

As aging progresses, the quality of DNA and proteins inside cells declines, which is known to be the cause of various ...

The ability to correct disease-causing genetic mistakes using genome editors holds great promise in medicine, but it is not without risk. When this type of "genetic surgery" is performed on DNA, for ...

Researchers at San Diego State University and Michigan State University are shedding new light on how viruses meticulously ...

Using artificial intelligence, MIT researchers have come up with a new way to design nanoparticles that can more efficiently ...

In 1957, just four years after Francis Crick and other scientists solved the riddle of DNA’s structure—the now famous double ...

Since 2008, the FDA has approved 11 treatments for a rare genetic condition called hereditary angioedema (HAE), three of ...

To our immune system, naked RNA is a sign of a viral or bacterial invasion and must be attacked. But our own cells also have RNA.

Waltham, Massachusetts–based Skyhawk Therapeutics has been collecting collaborations with larger companies in spades since ...

A previously unknown virus in farmed Pacific oysters may hold the key to mass die-offs in the multimillion-dollar industry, according to research from the University of British Columbia (UBC) in ...